Jonathan Wong
BSc, MD
Investigator, BC Children's Hospital
Pediatrics
Alshaikh, B.N. and Ting, J. and Lee, S. and Lemyre, B. and Wong, J. and Afifi, J. and Beltempo, M. and Shah, P.S. and Kanungo, J. and Cieslak, Z. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Aziz, K. and Fajardo, C. and Bodani, J. and Strueby, L. and Seshia, M. and Louis, D. and Alvaro, R. and Mukerji, A. and Da Silva, O. and Augustine, S. and Lee, K.-S. and Ng, E. and Daboval, T. and Khurshid, F. and Bizgu, V. and Barrington, K. and Lapoint, A. and Ethier, G. and Drolet, C. and Piedboeuf, B. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and Canning, R. and Makary, H. and Ojah, C. and Monterrosa, L. and Emberley, J. and Kajetanowicz, A. and Lee, S.K.
DOI: 10.1542/peds.2024-069102Journal of Pediatrics
Lipp, R. and Beltempo, M. and Lodha, A. and Weisz, D. and McKanna, J. and Matthews, I. and Ricci, M.F. and Hicks, M. and Benlamri, A. and Mukerji, A. and Alvaro, R. and Ng, E. and Luu, T.M. and Shah, P.S. and Abou Mehrem, A. and Pillay, T. and Wong, J. and Stavel, M. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Ting, J. and Fajardo, C. and Harabor, A. and Strueby, L. and Seshia, M. and Louis, D. and Ruth, C. and Yi, A. and Da Silva, O. and Augustine, S. and Lee, K.-S. and Lemyre, B. and Khurshid, F. and Bizgu, V. and Nouraeyan, N. and Barrington, K. and Lapointe, A. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and Barbosa de Oliveira, C. and Makary, H. and de Carvalho Nunes, G. and Alburaki, W. and Hudson, J.-A. and Afifi, J. and Kajetanowicz, A. and Piedboeuf, B. and Whittle, W. and Agarwal, S. and Lim, K. and Liauw, J. and El-Chaar, D. and Theriault, K. and Roy-Lacroix, M.-?. and Butt, K. and O'Quinn, C. and Pylypjuk, A.C. and Boucoiran, I. and Taillefer, C. and Crane, J. and Abenhaim, H. and Smith, G. and Wou, K. and Chandra, S. and Ubhi, J. and Figueiro-Filho, E. and Helewa, M. and Grigoriu, A. and Gratton, R. and Chan, C. and de Caralho Nunes, G. and Porto, L. and Melamed, N. and Burrows, J. and Wesson, L. and MacLellan, E. and Hayward, J. and Allen, V. and VanDyk, J. and Moodley, A. and Hendson, L. and Reichert, A. and Shafey, A. and Moddemann, D. and de Cabo, C. and Seesahai, J. and McKnight, S. and Coughlin, K. and Ly, L. and Raghuram, K. and Thomas, K. and Banihani, R. and Nguyen, K.-A. and Khairy, M. and Garfinkle, J. and Morin, A. and Blanger, S.
DOI: 10.1016/j.jpeds.2024.114270Ssrn
Gurram, S. and Fajardo, C.A. and Lee, K.-S. and da Silva, O. and Lemyre, B. and Yoon, E.W. and Shah, P.S. and Mohammad, K. and Shah, P.S. and Beltempo, M. and Kanungo, J. and Wong, J. and Stavel, M. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Ting, J. and Harabor, A. and Strueby, L. and Seshia, M. and Louis, D. and Alvaro, R. and Yi, A. and Mukerji, A. and Augustine, S. and Ng, E. and Lemyre, B. and Khurshid, F. and Bizgu, V. and Barrington, K. and Lapointe, A. and Ethier, G. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and de Oliveira, C.B. and Makary, H. and Ojah, C. and Newman, A. and Hudson, J.-A. and Afifi, J. and Kajetanowicz, A. and Piedboeuf, B. and Whittle, W. and Agarwal, S. and Lim, K. and Liauw, J. and El-Chaar, D. and Theriault, K. and Roy-Lacroix, M.-?. and Butt, K. and O?Quinn, C. and Pylypjuk, C. and Boucoiran, I. and Taillefer, C. and Crane, J. and Abenhaim, H. and Smith, G. and Wou, K. and Chandra, S. and Ubhi, J. and Figueiro-Filho, E. and Helewa, M. and Grigoriu, A. and Gratton, R. and Chan, C. and de Caralho Nunes, G. and Porto, L. and Melamed, N. and Burrows, J. and Wesson, L. and MacLellan, E. and Hayward, J. and Allen, V.
DOI: 10.2139/ssrn.5275671Frontiers in Pediatrics
Gette, F. and Aziz Ali, S. and Ho, M.S.P. and Richter, L.L. and Chan, E.S. and Yang, C.L. and Kieran, E. and Mammen, C. and Roberts, A. and Kang, K.T. and Wong, J. and Rassekh, S.R. and Castaldo, M. and Harris, K.C. and Lee, J. and Lam, C.K.L. and Chan, N.H. and Lisonkova, S. and Ting, J.Y.
DOI: 10.3389/fped.2025.1565897Neonatology
Taylor, R.S. and Singh, B. and Mukerji, A. and Dorling, J. and Alvaro, R. and Lodha, A. and El-Naggar, W. and Yoon, E.W. and Shah, P.S. and Beltempo, M. and Pillay, T. and Wong, J. and Stavel, M. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Fajardo, C. and Harabor, A. and Strueby, L. and Seshia, M. and Louis, D. and Ruth, C. and Silva, O.D. and Augustine, S. and Lee, K.-S. and Ng, E. and Lemyre, B. and Bizgu, V. and Barrington, K. and Lapointe, A. and Ethier, G. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and Oliveira, C.B.D. and Makary, H. and Nunes, G.D.C. and Alburaki, W. and Hudson, J.-A. and Afifi, J. and Kajetanowicz, A. and Piedboeuf, B.
DOI: 10.1159/000540278Acta Paediatrica International Journal of Paediatrics
Abda, A. and Yoon, E. and Kanungo, J. and Ojah, C. and Lapointe, A. and Shah, P.S. and Beltempo, M. and Barrington, K.J. and Pillay, T. and Wong, J. and Stavel, M. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Ting, J. and Fajardo, C. and Harabor, A. and Strueby, L. and Seshia, M. and Louis, D. and Ruth, C. and Yi, A. and Mukerji, A. and Da Silva, O. and Augustine, S. and Lee, K.-S. and Ng, E. and Lemyre, B. and Khurshid, F. and Bizgu, V. and Ethier, G. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and de Oliveira, C.B. and Makary, H. and de Carvalho Nunes, G. and Alburaki, W. and Hudson, J.-A. and Afifi, J. and Kajetanowicz, A. and Piedboeuf, B.
DOI: 10.1111/apa.17444Pediatric Infectious Disease Journal
Balay, C. and Kuan, M.T.Y. and Chao, M.J. and Richter, L.L. and Lee, K.-S. and Dunn, M.S. and Choudhury, J. and Afifi, J. and Slayter, K. and Bodani, J. and Minion, J. and Elsharkawy, A. and Landry, M.-A. and Toye, J. and Lisboa, L.F. and Read, B. and Gupta-Bhatnagar, S. and Khan, S. and Hamilton, C. and Srigley, J.A. and Shah, P.S. and Ting, J.Y. and Beltempo, M. and Pillay, T. and Wong, J. and Stavel, M. and Sherlock, R. and Mehrem, A.A. and Fajardo, C. and Harabor, A. and Strueby, L. and Seshia, M. and Ruth, C. and Mukerji, A. and Da Silva, O. and Augustine, S. and Ng, E. and Lemyre, B. and Khurshid, F. and Bizgu, V. and Nouraeyan, N. and Barrington, K. and Lapointe, A. and Ethier, G. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Costa, P. and Makary, H. and Aziz, A. and De Carvalho Nunes, G. and Alburaki, W. and Hudson, J.-A. and Kajetanowicz, A. and Chan, B. and Piedboeuf, B.
DOI: 10.1097/INF.0000000000004938Pediatrics
Mukerji, A. and Read, B. and Yang, J. and Baczynski, M. and Ng, E. and Dunn, M. and Ethier, G. and Mehrem, A.A. and Beltempo, M. and Drolet, C. and da Silva, O. and Louis, D. and Lemyre, B. and Afifi, J. and Singh, B. and Sherlock, R. and Stavel, M. and Masse, E. and Kanungo, J. and Wong, J. and Bodani, J. and Khurshid, F. and Lee, K.-S. and Augustine, S. and de Oliveira, C.B. and Makary, H. and Newman, A. and Ojah, C. and Shah, P.S.
DOI: 10.1542/peds.2023-064045Pediatrics
Garfinkle, J. and Khairy, M. and Simard, M.-N. and Wong, J. and Shah, P.S. and Luu, T.M. and Beltempo, M.
DOI: 10.1542/peds.2023-063654Journal of Pediatrics
Yeung, T. and Ahmed, A. and Wong, J. and Toye, J. and Abou Mehrem, A. and Mukerji, A. and Lapointe, A. and Ng, E. and Beltempo, M. and Pechlivanoglou, P. and Lee, S. and Shah, P.S. and Whittle, W. and Agarwal, S. and Lim, K. and El-Chaar, D. and Theriault, K. and Roy-Lacroix, M.-?. and Butt, K. and O'Quinn, C. and Pylypjuk, C. and Boucoiran, I. and Taillefer, C. and Crane, J. and Abenhaim, H. and Smith, G. and Wou, K. and Chandra, S. and Ubhi, J. and Figueiro-Filho, E. and Helewa, M. and Grigoriu, A. and Gratton, R. and Chan, C. and de Caralho Nunes, G. and Porto, L. and Melamed, N. and Burrows, J. and Augustine, S. and Wesson, L. and MacLellan, E. and Hayward, J. and Allen, V.
DOI: 10.1016/j.jpeds.2023.113863Journal of Pediatrics
Abou Mehrem, A. and Toye, J. and Beltempo, M. and Aziz, K. and Bizgu, V. and Wong, J. and Singhal, N. and Shah, P.S.
DOI: 10.1016/j.jpeds.2024.113976Archives of Disease in Childhood: Fetal and Neonatal Edition
Gurram Venkata, S.K.R. and Lodha, A. and Hicks, M. and Jain, A. and Lapointe, A. and Makary, H. and Kanungo, J. and Lee, K.-S. and Ye, X. and Shah, P.S. and Soraisham, A.S. and Beltempo, M. and Wong, J. and Stavel, M. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Ting, J. and Fajardo, C. and Bodani, J. and Strueby, L. and Seshia, M. and Louis, D. and Alvaro, R. and Yi, A. and Mukerji, A. and Da Silva, O. and Augustine, S. and Ng, E. and Lemyre, B. and Daboval, T. and Khurshid, F. and Bizgu, V. and Barrington, K. and Ethier, G. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and De Oliveira, C.B. and Ojah, C. and Newman, A. and Hudson, J.-A. and Afifi, J. and Kajetanowicz, A. and Piedboeuf, B. and Dahlgren, L. and Wood, S. and Metcalfe, A. and O'Quinn, C. and Helewa, M. and Taboun, F. and Melamed, N. and Abenhaim, H. and Wou, K. and Gratton, R. and Boucoiran, I. and Taillefer, C. and Theriault, K. and Allen, V. and Pillay, T. and VanDyk, J. and Moodley, A. and Hendson, L. and Benlamri, A. and Reichert, A. and Shafey, A. and Moddemann, D. and De Cabo, C. and Seesahai, J. and McKnight, S. and Coughlin, K. and Ly, L. and Raghuram, K. and Thomas, K. and Banihani, R. and Nguyen, K.-A. and Khairy, M. and Garfinkle, J. and Luu, T.M. and Morin, A. and Blanger, S.
DOI: 10.1136/archdischild-2023-325418Journal of Pediatrics
Melamed, N. and Weitzner, O. and Church, P. and Banihani, R. and Barrett, J. and Yang, J. and Wong, J. and Piedboeuf, B. and Shah, P.S. and Beltempo, M. and Kanungo, J. and Stavel, M. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Ting, J. and Fajardo, C. and Bodani, J. and Strueby, L. and Seshia, M. and Louis, D. and Alvaro, R. and Mukerji, A. and Da Silva, O. and Augustine, S. and Lee, K.-S. and Ng, E. and Lemyre, B. and Daboval, T. and Khurshid, F. and Bizgu, V. and Barrington, K. and Lapointe, A. and Ethier, G. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and Mehdizadeh-Hakak, H. and Makary, H. and Ojah, C. and Hudson, J.-A. and Afifi, J. and Aslam, A. and Lee, S.K. and Abenhaim, H. and Andrews, J. and Armson, A. and Audibert, F. and Aziz, K. and Ballantyne, M. and Berard, A. and Blais, L. and Bocking, A. and Burrows, J. and Butt, K. and Canning, R. and Carson, G. and Chaillet, N. and Chandra, S. and Cieslak, Z. and Coughlin, K. and Crane, J. and Creighton, D. and Dahlgren, L. and Daspal, S. and de Cabo, C. and Deshpandey, A. and Dow, K. and Dunn, M. and Helou, S.E. and El-Chaar, D. and El-Naggar, W. and Foster, J. and Gagnon, R. and Gratton, R. and Han, V. and Harrison, A. and Hasan, S. and Helewa, M. and Hicks, M. and Joseph, K.S. and Kajetanowicz, A. and Kalapesi, Z. and Khairy, M. and Lacaze-Masmonteil, T. and Lodha, A. and Luu, T.M. and Ly, L. and Majnemer, A. and Marc, I. and McDonald, S.D. and McMillan, D. and Metcalfe, A. and Moddemann, D. and Monterrosa, L. and Morais, M. and Mundle, W. and Murphy, L. and Murphy, K. and Nuyt, A.-M. and Nwaesei, C. and O'Brien, K. and Offringa, M. and Ouellet, A. and Pasquier, J.-C. and Pechlivanoglou, P. and Pelausa, E. and Portales-Casamar, E. and Premji, S. and Puligandla, P. and Pullenayegum, E. and Reichert, A. and Robson, K. and Schneider, C. and Shah, V. and Shivananda, S. and Singhal, N. and Skarsgard, E. and Skoll, A. and Smith, G. and Synnes, A. and Thriault, K. and Tough, S. and Ubhi, J. and Vincer, M. and Whittle, W. and Whyte, H. and Wilson, D. and Wood, S. and Ye, P. and Yee, W. and Zwicker, J. and Pillay, T. and Synnes, A. and Colby, L. and Anson, S. and Moodley, A. and Hendson, L. and Ricci, M.F. and McKnight, S. and Kelly, E. and Raghuram, K. and Thomas, K. and Nguyen, K.-A. and Mandel, R. and Morin, A. and Blanger, S.
DOI: 10.1016/j.jpeds.2023.02.021Journal of Perinatology
Afifi, J. and Shah, P.S. and Ye, X.Y. and Shah, V. and Piedboeuf, B. and Barrington, K. and Kelly, E. and El-Naggar, W. and Shah, P. and Beltempo, M. and Kanungo, J. and Wong, J. and Cieslak, Z. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Aziz, K. and Ting, J. and Fajarado, C. and Bodani, J. and Strueby, L. and Seshia, M. and Louis, D. and Alvaro, R. and Mukerji, A. and Da Silva, O. and Augustine, S. and Lee, K.-S. and Ng, E. and Lemyre, B. and Daboval, T. and Khurshid, F. and Bizgu, V. and Lapointe, A. and Ethier, G. and Drolet, C. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and Canning, R. and Makary, H. and Ojah, C. and Emberley, J. and Kajetanowicz, A. and Lee, S.K.
DOI: 10.1038/s41372-022-01483-6Journal of Perinatology
Lemyre, B. and Lacaze-Masmonteil, T. and Shah, P.S. and Bodani, J. and Doucette, S. and Dunn, M. and Louis, D. and Monterrosa, L. and Mukerji, A. and Schmlzer, G.M. and Singh, B. and Wong, J. and Ye, X.Y. and Offringa, M.
DOI: 10.1038/s41372-022-01346-0Journal of Perinatology
Ting, J.Y. and Yoon, E.W. and Fajardo, C.A. and Daboval, T. and Bertelle, V. and Shah, P.S. and Shah, P.S. and Beltempo, M. and Kanungo, J. and Wong, J. and Cieslak, Z. and Sherlock, R. and Mehrem, A.A. and Toye, J. and Ting, J.Y. and Bodani, J. and Strueby, L. and Seshia, M. and Louis, D. and Alvaro, R. and Mukerji, A. and Da Silva, O. and Augustine, S. and Lee, K.-S. and Ng, E. and Lemyre, B. and Daboval, T. and Khurshid, F. and Bizgu, V. and Barrington, K. and Lapointe, A. and Ethier, G. and Drolet, C. and Piedboeuf, B. and Claveau, M. and St-Hilaire, M. and Bertelle, V. and Masse, E. and Canning, R. and Makary, H. and Ojah, C. and Monterrosa, L. and Emberley, J. and Afifi, J. and Kajetanowicz, A. and Lee, S.K.
DOI: 10.1038/s41372-022-01382-wChild's Nervous System
Gurram Venkata, S.K.R. and Shah, P.S. and Beltempo, M. and Yoon, E. and Wood, S. and Hicks, M. and Daboval, T. and Wong, J. and Wintermark, P. and Mohammad, K.
DOI: 10.1007/s00381-022-05575-8Journal of Perinatology
Read, B. and Ethier, G. and Mehrem, A.A. and Dunn, M. and Pelletier-Veilleux, S. and Davidson, J. and Yoder, B. and Gigolyk, S. and Alvaro, R. and Yi, A. and Sheldon, J. and Lemyre, B. and Faulkner, M. and Daboval, T. and McInnis, S. and Canning, R. and Makary, H. and Stevens, J. and Eastland, L. and Singh, B. and Afifi, J. and Lai, G. and Zeid, M. and Claveau, M. and Bodani, J. and Hrynowetsky, D. and Wong, J. and Zarembo, M. and Thiel, C. and Buettner, A. and Sherlock, R. and Kajla, R. and Amyotte, M. and McKanna, J. and Daeglish, S. and Drolet, C. and Taylor, R. and Bahan, K. and Hawes, J. and Kang, S. and Khurshid, F. and McGregor, H. and Coughlin, K. and Coughlin, K. and Shah, V. and Baczynski, M. and Augustine, S. and Szekely, T. and Yuen, R. and Bailey, C. and Aslam, A. and Masse, E. and Grodin, K. and Savanh, P. and Bartholomew, J. and Stavel, M. and al Mudaffer, M. and Shah, P.S. and Ting, J. and Seshia, M. and Louis, D. and Barrington, K. and Drolet, C. and Mukerji, A.
DOI: 10.1038/s41372-022-01395-5Frontiers in Pediatrics
Khurshid, F. and Coo, H. and Khalil, A. and Messiha, J. and Ting, J.Y. and Wong, J. and Shah, P.S.
DOI: 10.3389/fped.2021.759776Simulation in Healthcare
Wong, J. and Kalaniti, K. and Castaldo, M. and Whyte, H. and Lee, K.-S. and Schroff, M. and Campbell, D.M.
DOI: 10.1097/SIH.0000000000000479Paediatrics and Child Health (Canada)
Lemyre, B. and Bodani, J.P. and Doucette, S. and Dunn, M.S. and Louis, D. and Monterrosa, L. and Mukerji, A. and Schmlzer, G.M. and Shah, P. and Singh, B. and Wong, J. and Lacaze-Masmonteil, T. and Offringa, M.
DOI: 10.1093/pch/pxz160Journal of Clinical Neonatology
DOI: 10.4103/jcn.jcn_110_18Cureus
Jonathan Wong and Emer Finan and Douglas Campbell
DOI: 10.7759/cureus.144807 / 2017
Journal of Perinatology
Stavel, M. and Wong, J. and Cieslak, Z. and Sherlock, R. and Claveau, M. and Shah, P.S.
DOI: 10.1038/jp.2016.196American Journal of Perinatology
Wong, J. and Shah, P.S. and Yoon, E.W. and Yee, W. and Lee, S. and Dow, K.
DOI: 10.1055/s-0034-1371703American Journal of Perinatology
Wong, J. and Dow, K. and Shah, P. and Andrews, W. and Lee, S.
DOI: 10.1055/s-0032-1311978Toronto Notes, 25th edition
Bhatti A, Mansfield A and Wong J. Respirology. In: Lam D and Dugani S, eds. Toronto Notes. 25th ed. Toronto, Ontario; Type and Graphics, 2009.
Thorax
Yuan, R. and Hogg, J.C. and Par, P.D. and Sin, D.D. and Wong, J.C. and Nakano, Y. and McWilliams, A.M. and Lam, S. and Coxson, H.O.
DOI: 10.1136/thx.2008.112433Progress in Biomedical Optics and Imaging - Proceedings of SPIE
Wong, J.C. and Nakano, Y. and Coxson, H.O. and Mller, N.L. and Par, P.D. and Hogg, J.C.
DOI: 10.1117/12.769697European Respiratory Journal
de Jong, P.A. and Long, F.R. and Wong, J.C. and Merkus, P.J. and Tiddens, H.A. and Hogg, J.C. and Coxson, H.O.
DOI: 10.1183/09031936.06.00070805Magnetic Resonance in Medicine
Woods, J.C. and Choong, C.K. and Yablonskiy, D.A. and Bentley, J. and Wong, J. and Pierce, J.A. and Cooper, J.D. and Macklem, P.T. and Conradi, M.S. and Hogg, J.C.
DOI: 10.1002/mrm.21076American Journal of Respiratory and Critical Care Medicine
Nakano, Y. and Wong, J.C. and De Jong, P.A. and Buzatu, L. and Nagao, T. and Coxson, H.O. and Elliott, W.M. and Hogg, J.C. and Par, P.D.
DOI: 10.1164/rccm.200407-874OCNon-invasive ventilation is being used commonly amongst preterm infants, and there is increasing use of non-invasive high frequency ventilation. We are conducting a study to better understand how this mode of ventilation helps infants as compared to another commonly used mode, which is continuous positive airway pressure (CPAP). We are able to do this through measuring the electrical activity of the diaphragm, and by this method better understand how these different modes of ventilation affect how a baby breaths.
Simulation is being increasingly used in medical education. It is effective in improving knowledge and in many fields has been associated with improved performance. Simulation is being considered not only for delivery of education but also for assessment. Before such a tool is used routinely in neonatal training across Canada, it is important to understand its current usage by accredited training programs. Therefore, we are conducting a survey to program directors and fellows across all neonatal training programs in Canada.
Our sickest patients often require transport from the NICU to different parts of the hospital for investigations that help guide their care. The transport process is complex with the potential for latent safety threats to be present. This project uses simulation to recreate that process of going from the NICU to receive an MRI in order those safety threats. By doing this, we are working to make change to how we perform transports in order to prevent errors from happening and better understand how we can safely conduct neonatal intramural transports.
Creative Professional Research Grant, Hospital for Sick Children- 2016
Mallinckrodt Young Investigator Research Fund Award - 2015
Physicians’ Services Incorporated Foundation Resident Research Prize, Queen’s University, Postgraduate Medical Education - 2012
Resident Research Competition Award, Queen’s University, Department of Pediatrics - 2010, 2011, 2012
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